SYSTEMIC DELIVERY OF ADENO-ASSOCIATED VIRUS VECTOR EXPRESSING GAMMA-SARCOGLYCAN AND THE TREATMENT OF MUSCULAR DYSTROPHY

Number of patents in Portfolio can not be more than 2000

United States of America

APP PUB NO 20240374684A1
SERIAL NO

18444018

Stats

ATTORNEY / AGENT: (SPONSORED)

Importance

Loading Importance Indicators... loading....

Abstract

See full text

Described herein are methods of treating muscular dystrophy comprising administering a recombinant AAV (rAAV) scAAVrh74.MHCK7.hSGCG vector, methods of expressing gamma-sarcoglycan gene in a patient, pharmaceutical compositions comprising the rAAV, and methods of generating the rAAV.

Loading the Abstract Image... loading....

First Claim

See full text

Family

Loading Family data... loading....

Patent Owner(s)

Patent OwnerAddress
SAREPTA THERAPEUTICS INC215 FIRST STREET CAMBRIDGE MA 02142

International Classification(s)

Inventor(s)

Inventor Name Address # of filed Patents Total Citations
POZSGAI, Eric Cambridge, US 3 1
RODINO-KLAPAC, Louise Cambridge, US 33 56

Cited Art Landscape

Load Citation

Patent Citation Ranking

Forward Cite Landscape

Load Citation